Inspired by the Patients We Serve
Spark® Therapeutics Medical Affairs is committed to providing healthcare professionals with medical information and education that supports appropriate patient care.
Who we are
Our team of healthcare professionals maintains an active dialogue with the scientific community. We are driven by the urgent needs of patients and the challenges before us—which demand uncompromising focus, tenacity and determination.
What we do
Our team seeks to actively engage with physicians, researchers, and other healthcare professionals to provide education about the field of gene therapy. We respond to inquiries about our programs and therapeutic areas as well as related genetic disorders.
Our scientific platforms and programs
Spark uses adeno-associated viral (AAV) vectors to advance research programs against cell targets in the retina, liver, and central nervous system. Explore our clinical pipeline of investigative research programs, including inherited retinal diseases (IRDs), hematologic and lysosomal storage disorders, and neurodegenerative diseases.
